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  • female doctor explaining the treatment
    News releases

    Could an existing antibiotic be used to treat rare liver disease?

    A new international clinical trial funded by medical research organisation LifeArc will test whether oral vancomycin, an existing antibiotic, could…

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  • Person's hands popping out an oral antibiotic from a packet.

    VITALITY Trial: Repurposing an existing antibiotic for PSC-IBD 

    VITALITY Trial: Repurposing an existing antibiotic for PSC-IBD  We’re supporting a Phase 2b/3 clinical trial to investigate whether the oral…

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  • Young girl lying on a hospital bed undergoing kidney ultrasound
    News releases

    New study brings hope for children with rare life-threatening kidney disease

    We’re proud to have funded new research with Great Ormond Street Hospital Charity (GOSH Charity) and Kidney Research UK that…

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  • Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases

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  • Investigating a novel gene therapy for CTLA-4 insufficiency

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  • Evaluation of the effect of intranasal insulin on development and behaviour in Phelan-McDermid syndrome

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  • Advancing Repurposed Therapeutics for Epidermolysis Bullosa (ART-EB)

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  • Young Boy Having Fun In Garden Chasing And Bursting Bubbles
    News releases

    Introducing Raremap: a new way to navigate the rare disease landscape 

    LifeArc has collaborated with Rare Disease Research UK to launch Raremap, the UK’s first directory of rare disease organisations.   There’s a vibrant…

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  • Scientists working and having discussions about working in laboratory
    News releases

    New boost for personalised rare disease treatments as the Rare Therapies Launch Pad becomes part of LifeArc

    We will be integrating the Rare Therapies Launch Pad (RTLP) into our organisation, marking an important next step in efforts…

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  • a blue chromosome DNA and gradually glowing flicker light matter chemical when camera moving closeup.
    News releases

    World-first gene therapy to target devastating rare immune disorder

    A first-of-its-kind gene therapy to treat people with CTLA-4 insufficiency, a rare and life-limiting inherited immune disorder, is being advanced…

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  • Investigating a novel gene therapy for CTLA-4 insufficiency

    Investigating a novel gene therapy for CTLA-4 insufficiency We’re funding a pioneering programme and clinical trial, led by Dr Thomas Fox…

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  • Elpida Therapeutics patient hugging his mum in a playground

    Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases

    Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases We’ve partnered with Elpida Therapeutics to advance the clinical development of…

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