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    Rare Disease Clinical Trials Programme

    Rare Disease Clinical Trials Programme The Rare Disease Clinical Trials Programme has been set up to progress innovations that could…

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    Articles, News releases

    LifeArc joins the REMEDi4ALL Consortium, a pioneering global platform shaping the future of drug repurposing

    LifeArc and the EU-funded project, REMEDi4ALL, have announced a collaboration agreement to strengthen the partnership’s potential to transform and accelerate…

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  • Doctor performs joint checks on person with Muscular dystrophy by touching their calf.
    News releases

    £1 million partnership aims to develop new treatments for congenital muscular dystrophy

    Researchers from University College London have jointly received a £1 million grant from LifeArc and Muscular Dystrophy UK, to develop…

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  • Muscular Dystrophy UK: A £1 million partnership to find new treatments for congenital muscular dystrophy

    Muscular Dystrophy UK: A £1 million partnership to find new treatments for congenital muscular dystrophy We’ve partnered with Muscular Dystrophy…

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  • Close up of a doctor's hands pointing at an image of a brain scan

    DefINe: A clinical trial to explore treatment for a rare genetic brain disorder 

    DefINe: A clinical trial to explore treatment for a rare genetic brain disorder  The DefINe trial, launched by the University…

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  • Prospective evaluation of KARSARC -a gene expression-based risk classifier for patients with soft tissue sarcomas treated with pazopanib

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  • FARGO: FAecal Microbiota Transplantation in primaRy sclerosinG chOlangitis

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  • TIARA: Autologous Tregs for Aplastic Anaemia

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  • The CADET Trail: The Children’s Adaptive Deep brain stimulation for Epilepsy Trial

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  • STOPFOP: Saracatinib trial TO Prevent FOP

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  • Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type II

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  • Phase II Study of a Novel Vitamin Metabolite (CoA-Z) for Pantothenate Kinase Associated Neurodegeneration

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