General Archive

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News releasesIntroducing Raremap: a new way to navigate the rare disease landscape
LifeArc has collaborated with Rare Disease Research UK to launch Raremap, the UK’s first directory of rare disease organisations. There’s a vibrant…
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News releasesNew boost for personalised rare disease treatments as the Rare Therapies Launch Pad becomes part of LifeArc
We will be integrating the Rare Therapies Launch Pad (RTLP) into our organisation, marking an important next step in efforts…
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News releasesWorld-first gene therapy to target devastating rare immune disorder
A first-of-its-kind gene therapy to treat people with CTLA-4 insufficiency, a rare and life-limiting inherited immune disorder, is being advanced…
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Investigating a novel gene therapy for CTLA-4 insufficiency
Investigating a novel gene therapy for CTLA-4 insufficiency We’re funding a pioneering programme and clinical trial, led by Dr Thomas Fox…
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Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases
Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases We’ve partnered with Elpida Therapeutics to advance the clinical development of…
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News releasesLifeArc announces partnership with Elpida Therapeutics to accelerate gene therapies for ultra-rare diseases in children
We have announced a new partnership with Elpida Therapeutics to support the development of three gene therapy programmes targeting ultra-rare…
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Hunter syndrome: A clinical trial to test pioneering gene therapy
Hunter syndrome: A clinical trial to test pioneering gene therapy We’re co-funding a first-in-human clinical trial with the University of Manchester…
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CADET Trial: Advancing deep brain stimulation for rare childhood epilepsy
CADET Trial: Advancing deep brain stimulation for rare childhood epilepsy We’ve partnered with GOSH Charity to fund an innovative clinical…
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LifeArc & Genetic Alliance UK – More trials, better data, faster access policy report
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Nasal insulin trial: exploring a new treatment option for Phelan-McDermid Syndrome
Nasal insulin trial: exploring a new treatment option for Phelan-McDermid Syndrome We’re funding a major clinical trial to discover whether…
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News releasesCould a nasal insulin spray improve the lives of children and young people living with a rare condition?
We are funding a new multi-million pound trial that will reveal if a simple nasal spray could improve daily life…
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News releasesLifeArc-funded trial gives new hope for children with devastating rare genetic disorder
The parents of a three-year-old boy born with a devastating, life-limiting genetic condition say they are now excited for his…
