General Archive
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Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases
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Investigating a novel gene therapy for CTLA-4 insufficiency
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Evaluation of the effect of intranasal insulin on development and behaviour in Phelan-McDermid syndrome
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Advancing Repurposed Therapeutics for Epidermolysis Bullosa (ART-EB)
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News releasesIntroducing Raremap: a new way to navigate the rare disease landscape
LifeArc has collaborated with Rare Disease Research UK to launch Raremap, the UK’s first directory of rare disease organisations. There’s a vibrant…
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News releasesNew boost for personalised rare disease treatments as the Rare Therapies Launch Pad becomes part of LifeArc
We will be integrating the Rare Therapies Launch Pad (RTLP) into our organisation, marking an important next step in efforts…
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News releasesWorld-first gene therapy to target devastating rare immune disorder
A first-of-its-kind gene therapy to treat people with CTLA-4 insufficiency, a rare and life-limiting inherited immune disorder, is being advanced…
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Investigating a novel gene therapy for CTLA-4 insufficiency
Investigating a novel gene therapy for CTLA-4 insufficiency We’re funding a pioneering programme and clinical trial, led by Dr Thomas Fox…
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Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases
Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases We’ve partnered with Elpida Therapeutics to advance the clinical development of…
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News releases
LifeArc announces partnership with Elpida Therapeutics to accelerate gene therapies for ultra-rare diseases in children
We have announced a new partnership with Elpida Therapeutics to support the development of three gene therapy programmes targeting ultra-rare…
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Hunter syndrome: A clinical trial to test pioneering gene therapy
Hunter syndrome: A clinical trial to test pioneering gene therapy We’re co-funding a first-in-human clinical trial with the University of Manchester…
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CADET Trial: Advancing deep brain stimulation for rare childhood epilepsy
CADET Trial: Advancing deep brain stimulation for rare childhood epilepsy We’ve partnered with GOSH Charity to fund an innovative clinical…