General Archive

Home » Rare disease
  • LifeArc Translational Centres for Rare Diseases

    LifeArc Translational Centres for Rare Diseases We have invested £40 million into 4 Translational Centres for Rare Diseases, to unlock…

    Read more

  • A female LifeArc scientist loads a plate into a lab machine
    News releases

    First-of-a-kind plan announced to get more children access to cutting-edge, proven gene therapy treatments for rare diseases

    Great Ormond Street Hospital (GOSH), supported by LifeArc and Great Ormond Street Hospital Children’s Charity (GOSH Charity), is announcing its…

    Read more

  • LifeArc-CSO fund for Scottish translational researchers

    LifeArc-CSO fund for Scottish translational researchers In association with the Chief Scientist Office (CSO) for the Scottish Government, we support…

    Read more

  • LifeArc gene therapy innovation fund

    LifeArc gene therapy innovation fund The LifeArc Gene Therapy Innovation Fund is a £5m annual fund to support manufacture of…

    Read more

  • Great Ormond Street Hospital entrance

    LifeArc and GOSH charity fund

    LifeArc and GOSH charity fund LifeArc and GOSH Charity support a joint funding scheme focused on helping GOSH researchers drive…

    Read more

  • 5 children of varied ethnicity stand outside smiling in a line with arms over each others' shoulders, the sun shining in the background.

    LifeArc and Action medical research fund

    LifeArc and Action medical research fund Action Medical Research and LifeArc want to improve the lives of children suffering from…

    Read more

  • LifeArc Philanthropic fund

    The LifeArc Philanthropic Fund The Fund provides grants and funding to academic researchers working to advance new treatments and diagnostics…

    Read more

  • Child affected by EB with her father. Photo ©Debra Austria

    Repurposing therapies for EB

    £2.5 million to develop therapeutics for Epidermolysis Bullosa (EB) LifeArc and DEBRA Austria are partnering to commit £2.5 million to…

    Read more

  • Translational rare disease centres

    Translational rare disease centres With this £40 million we aim to build on the UK’s rich, rare disease research base,…

    Read more

  • The gloved hands of a lab-coated scientist hold two vials and a pen above lab bench and a tray of vials.

    Muscular Dystrophy Translational Research Fund

    Muscular Dystrophy Translational Research Fund The Muscular Dystrophy Translational Research Fund is a joint fund created by LifeArc and Muscular…

    Read more

  • News releases

    LifeArc funds pivotal clinical trial to treat an ultra-rare genetic disease with possible link to leader of the mutiny on the Bounty in 1789

    A pivotal clinical trial to look at repurposing the UK-licensed medicine, deferiprone, for patients with neuroferritinopathy, an ultra-rare genetic disease…

    Read more

  • A scientist in a white lab coat pipettes liquid into a small vial.
    Articles & blogs

    6 challenges in rare disease research and how we can overcome them

    Rare conditions, individually, have low patient numbers. However, with more than 7,000 rare diseases identified, collectively there are millions of…

    Read more

WordPress development by Andy White using PorterWP