General Archive
-
News releasesLifeArc announces partnership with Elpida Therapeutics to accelerate gene therapies for ultra-rare diseases in children
We have announced a new partnership with Elpida Therapeutics to support the development of three gene therapy programmes targeting ultra-rare…
-
Hunter syndrome: A clinical trial to test pioneering gene therapy
Hunter syndrome: A clinical trial to test pioneering gene therapy We’re co-funding a first-in-human clinical trial with the University of Manchester…
-
CADET Trial: Advancing deep brain stimulation for rare childhood epilepsy
CADET Trial: Advancing deep brain stimulation for rare childhood epilepsy We’ve partnered with GOSH Charity to fund an innovative clinical…
-
LifeArc & Genetic Alliance UK – More trials, better data, faster access policy report
-
Nasal insulin trial: exploring a new treatment option for Phelan-McDermid Syndrome
Nasal insulin trial: exploring a new treatment option for Phelan-McDermid Syndrome We’re funding a major clinical trial to discover whether…
-
News releasesCould a nasal insulin spray improve the lives of children and young people living with a rare condition?
We are funding a new multi-million pound trial that will reveal if a simple nasal spray could improve daily life…
-
News releasesLifeArc-funded trial gives new hope for children with devastating rare genetic disorder
The parents of a three-year-old boy born with a devastating, life-limiting genetic condition say they are now excited for his…
-
The use of CARBALIVE in the treatment of cholestatic liver disease
-
News releasesBirmingham researchers lead world-first trial for rare liver disease treatment funded by LifeArc
University Hospitals Birmingham NHS Foundation Trust (UHB) has treated the first patient in an early-phase clinical trial investigating whether a…
-
ART-EB: An innovative drug repurposing trial to find treatments for a rare skin disorder
ART-EB: An innovative drug repurposing trial to find treatments for a rare skin disorder We’ve partnered with DEBRA UK to…
-
Transforming Diagnosis and Treatment: Rare Disease Summit
About the event The Rare Disease Summit will explore how the UK can accelerate progress in diagnosing those living with…
-
ArticlesLifeArc Pathfinder Award recipients uncover genetic cause of severe nerve condition in children
Researchers at the University of Manchester have identified a rare genetic mutation that causes severe nerve damage in children following mild infections. Their findings…