General Archive

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DefINe: A clinical trial to explore treatment for a rare genetic brain disorder
DefINe: A clinical trial to explore treatment for a rare genetic brain disorder The DefINe trial, launched by the University…
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Prospective evaluation of KARSARC -a gene expression-based risk classifier for patients with soft tissue sarcomas treated with pazopanib
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FARGO: FAecal Microbiota Transplantation in primaRy sclerosinG chOlangitis
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TIARA: Autologous Tregs for Aplastic Anaemia
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The CADET Trial: The Children’s Adaptive Deep brain stimulation for Epilepsy Trial
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STOPFOP: Saracatinib trial TO Prevent FOP
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Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type II
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Phase II Study of a Novel Vitamin Metabolite (CoA-Z) for Pantothenate Kinase Associated Neurodegeneration
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DefINe: A trial to test the use of deferiprone in people with neuroferritinopathy
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The TIARA trial: Investigating a new treatment for a life-threatening blood disorder
The TIARA trial: Investigating a new treatment for a life-threatening blood disorder A collaboration with the Aplastic Anaemia Trust to…
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Innovation Hubs for Gene Therapy: A national network to transform gene therapy research
Innovation Hubs for Gene Therapy: A national network to transform gene therapy research Our partnership with the Medical Research Council…
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GOSH and UCL: Co-funding a new blood test to detect a deadly heart condition in children
GOSH and UCL: Co-funding a new blood test to detect a deadly heart condition in children Researchers at UCL (University…
