Funding, projects and partnerships
We form strategic partnerships to advance promising research related to our focus areas.
We apply our disease knowledge, translational expertise, cutting-edge science, networks and funding to progress projects. If you’re interested in partnering with us, please get in touch.
Find details of our existing work and open funding calls below.
Projects
Featured projects
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Rare disease, Neurodegeneration
Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases
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Our science
Our Future Health: Accelerating health research using clinical data
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Childhood cancer
C-Further Consortium: advancing innovative cancer therapies for children and young people
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Global health, Antimicrobial resistance
PACE: A £30 million collaborative initiative to tackle antimicrobial resistance
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Chronic & rare respiratory
Translational Innovation Hub Network for Lung Health and Infection in Cystic Fibrosis project page
All projects
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Rare disease
Investigating a novel gene therapy for CTLA-4 insufficiency
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Rare disease, Neurodegeneration
Elpida Therapeutics: Accelerating gene therapies for ultra‑rare neurodegenerative diseases
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Rare disease
Hunter syndrome: A clinical trial to test pioneering gene therapy
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Rare disease
CADET Trial: Advancing deep brain stimulation for rare childhood epilepsy
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Rare disease
Nasal insulin trial: exploring a new treatment option for Phelan-McDermid Syndrome
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Rare disease
ART-EB: An innovative drug repurposing trial to find treatments for a rare skin disorder
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Rare disease
Rare Disease Clinical Trials Programme
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Rare disease
Muscular Dystrophy UK: A £1 million partnership to find new treatments for congenital muscular dystrophy
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Rare disease
DefINe: A clinical trial to explore treatment for a rare genetic brain disorder
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Rare disease
The TIARA trial: Investigating a new treatment for a life-threatening blood disorder
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Rare disease
Innovation Hubs for Gene Therapy: A national network to transform gene therapy research
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Rare disease
GOSH and UCL: Co-funding a new blood test to detect a deadly heart condition in children
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Rare disease
GOSH: A partnership to increase access to gene therapies for children with rare diseases
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Rare disease
Funding: Partnering with Great Ormond Street Hospital Charity (GOSH Charity) to deliver translational research accelerator grants
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Rare disease
LifeArc Translational Centres for Rare Disease
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Rare disease
The Pathfinder Award: Fast-tracking innovative rare disease research projects with £3 million of funding