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  • Close-up of a child's hand on the wheel of a wheelchair
    Articles

    LifeArc Pathfinder Award recipients uncover genetic cause of severe nerve condition in children  

    Researchers at the University of Manchester have identified a rare genetic mutation that causes severe nerve damage in children following mild infections. Their findings…

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  • Room with full audience and the Chair of our rare disease Translational Challenge, Amit Nathwani on stage.
    Articles

    LifeArc and Genetic Alliance UK launch a new report calling for the acceleration of research and development (R&D) for rare diseases  

    LifeArc and Genetic Alliance UK have launched a report calling for the UK Government, NHS, researchers, industry, patient groups and…

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  • Accelerating R&D for rare disease in the UK: An opportunity to change millions of lives 

    This report is a call to transform the UK’s rare disease future.  It outlines how we can smooth the rare…

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  • Female healthcare professional talking to a patient.

    Rare Disease Clinical Trials Programme

    Rare Disease Clinical Trials Programme The Rare Disease Clinical Trials Programme has been set up to progress innovations that could…

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  • Hands on top of each other to show team work
    Articles, News releases

    LifeArc joins the REMEDi4ALL Consortium, a pioneering global platform shaping the future of drug repurposing

    LifeArc and the EU-funded project, REMEDi4ALL, have announced a collaboration agreement to strengthen the partnership’s potential to transform and accelerate…

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  • Doctor performs joint checks on person with Muscular dystrophy by touching their calf.
    News releases

    £1 million partnership aims to develop new treatments for congenital muscular dystrophy

    Researchers from University College London have jointly received a £1 million grant from LifeArc and Muscular Dystrophy UK, to develop…

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  • Muscular Dystrophy UK: A £1 million partnership to find new treatments for congenital muscular dystrophy

    Muscular Dystrophy UK: A £1 million partnership to find new treatments for congenital muscular dystrophy We’ve partnered with Muscular Dystrophy…

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  • Close up of a doctor's hands pointing at an image of a brain scan

    DefINe: A clinical trial to explore treatment for a rare genetic brain disorder 

    DefINe: A clinical trial to explore treatment for a rare genetic brain disorder  The DefINe trial, launched by the University…

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  • Prospective evaluation of KARSARC -a gene expression-based risk classifier for patients with soft tissue sarcomas treated with pazopanib

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  • FARGO: FAecal Microbiota Transplantation in primaRy sclerosinG chOlangitis

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  • TIARA: Autologous Tregs for Aplastic Anaemia

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  • The CADET Trial: The Children’s Adaptive Deep brain stimulation for Epilepsy Trial

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